BioMarin, n-Lorem Partner to Develop First Investigational Therapy for ReNU Syndrome
BioMarin and the n-Lorem Foundation have partnered to develop an investigational antisense oligonucleotide therapy targeting the most common genetic variant associated with ReNU syndrome, a rare neurodevelopmental disorder with no approved treatments.
Dr. Nicola Whiffin | 28/07/2026 | By News Bureau
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