Last edition
News about "Enzyme replacement therapy"
JCR Pharmaceuticals secures its first international approval for Izcargo in the UAE, expanding access to its innovative blood-brain barrier-penetrating therapy for patients with Hunter syndrome and advancing rare disease treatment across the MENA region.
Enzyme Replacement Therapy | 23/07/2026 | By News Bureau
AskBio Doses First Participant in Phase 1/2 Trial for Pompe Disease Gene Therapy
AskBio has dosed the first participant in its Phase 1/2 PROGRESS-GT LOPD trial evaluating investigational gene therapy AB-1009 for late-onset Pompe disease, advancing research into potential long-term treatment solutions for the rare genetic disorder.
Enzyme Replacement Therapy | 14/05/2026 | By News Bureau
We use our own and third party cookies to produce statistical information and show you personalized advertising by analyzing your browsing, according to our COOKIES POLICY. If you continue visiting our Site, you accept its use.
More information: Privacy Policy