News about "Facioscapulohumeral Muscular Dystrophy "

Del-Brax from Novartis Achieves Primary Biomarker Endpoint in FSHD Study

Del-Brax from Novartis Achieves Primary Biomarker Endpoint in FSHD Study

Novartis reported positive phase 1/2 FORTITUDE study results for delpacibart braxlosiran (del-brax) in FSHD, meeting primary and key secondary biomarker endpoints. The therapy could become the first disease-modifying treatment for FSHD, with a phase 3 trial underway.

Facioscapulohumeral Muscular Dystrophy | 12/06/2026 | By News Bureau

Chugai Announces Discontinuation of Emugrobart Trials in SMA and FSHD

Chugai Announces Discontinuation of Emugrobart Trials in SMA and FSHD

Roche halts development after mid-stage trials fail to show consistent functional benefits, while obesity-focused trials continue amid promising scientific rationale.

Facioscapulohumeral Muscular Dystrophy | 25/03/2026 | By News Bureau 262


 

 

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