News about "Pediatric Clinical Trial "

Ascidian Therapeutics Completes STELLAR Trial Dose Escalation for ACDN-01 in Stargardt Disease

Ascidian Therapeutics Completes STELLAR Trial Dose Escalation for ACDN-01 in Stargardt Disease

Ascidian Therapeutics completes Phase 1/2 STELLAR dose escalation for ACDN-01 in Stargardt disease, advances pediatric enrollment, and launches STARPATH prescreening to accelerate clinical trial access.

Pediatric Clinical Trial | 05/05/2026 | By News Bureau

Pharming Unveils Positive Topline Data in Pediatric Clinical Trial of Leniolisib

Pharming Unveils Positive Topline Data in Pediatric Clinical Trial of Leniolisib

Pharming plans to include data from this 4-11-year-old trial in regulatory filings worldwide for the approval of leniolisib for pediatric patients with APDS, beginning in 2025.

Pediatric Clinical Trial | 13/12/2024 | By Aishwarya 333


 

 

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