News about "Pediatric HoFH"

EU Approves Chiesi's LOJUXTA for Pediatric HoFH Patients

EU Approves Chiesi's LOJUXTA for Pediatric HoFH Patients

The European Commission has approved Chiesi’s LOJUXTA (lomitapide) for children aged 5 years and older with Homozygous Familial Hypercholesterolaemia (HoFH), expanding treatment options for this ultra-rare genetic disorder.

Pediatric HoFH | 25/06/2026 | By News Bureau


 

 

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