News about "protein misfolding diseases"

Octant's OCT-980 Receives FDA Orphan Drug Designation for Retinitis Pigmentosa

Octant's OCT-980 Receives FDA Orphan Drug Designation for Retinitis Pigmentosa

Octant is evaluating OCT-980 in a Phase 1b/2 study at US sites, with the aim of developing a potential oral, disease-modifying treatment for RHO-adRP.

Protein Misfolding Diseases | 29/10/2026 | By News Bureau


 

 

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