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News about "rare disease"
Ionis Completes Enrollment in Phase 3 REVEAL Study for Angelman Syndrome
Ionis has completed enrollment in the pivotal Phase 3 REVEAL study of obudanersen for Angelman syndrome, with topline clinical trial results expected in the second half of 2027.
Rare Disease | 06/07/2026 | By Akanki
Chugai Pharma's Avastin Secures Approval in Japan for Additional Indication
Chugai Pharma’s Avastin has received approval in Japan for an additional indication, becoming the world’s first therapeutic option for neurofibromatosis type 2. The approval is supported by positive phase 2 clinical study results.
Rare Disease | 22/06/2026 | By News Bureau
Regel Therapeutics Names Stephen J. Farr as New CEO
Regel Therapeutics’ Board of Directors has named Stephen J. Farr, PhD, as the new Chief Executive Officer (CEO).
Rare Disease | 21/06/2024 | By Aishwarya | 393
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