News about " Rare Neuromuscular Junction Diseases"

Collaboration Aims to Scale AAV Manufacturing for Rare Neuromuscular Junction Diseases

Collaboration Aims to Scale AAV Manufacturing for Rare Neuromuscular Junction Diseases

NMJ disorders often cause severe muscle weakness, with many patients requiring respiratory support, wheelchairs, or tube feeding. These genetic diseases can be life-threatening, often diagnosed in childhood but sometimes appearing later in life.

Rare Neuromuscular Junction Diseases | 24/08/2025 | By Darshana


 

 

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