News about "San Raffaele Telethon Institute for Gene Therapy"

FDA Approves Waskyra Gene Therapy for Wiskott-Aldrich Syndrome

FDA Approves Waskyra Gene Therapy for Wiskott-Aldrich Syndrome

Fondazione Telethon announced that the US FDA has approved Waskyra (etuvetidigene autotemcel), a gene therapy for Wiskott-Aldrich Syndrome (WAS), marking a milestone in both science and clinical care. The approval offers new hope for patients living with this rare immunodeficiency disorder.

San Raffaele Telethon Institute For Gene Therapy | 11/12/2025 | By Akanki 162


 

 

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